Funding Of 2nd Generation Enzyme Replacement Therapy (ERT) Nexviazyme (avalglucosidase alfa) For Treating Pompe Disease

People with Pompe disease in NZ have had to rely on compassionate access to drugs, or participation in clinical trials. So, to have NZ finally acknowledging the worthiness of this drug is absolutely a game changer for those of us with Pompe, and those who ...